Which one of the following diseases or disorders has not been treated using gene therapy methods?
A) rheumatoid arthritis
B) familial hypercholesterolemia
C) cri du chat syndrome
D) cystic fibrosis
E) SCID

Question

Quizplus · Accepted Answer

Cri du chat syndrome is a chromosomal condition that results from a deletion of part of chromosome 5. Unlike the other conditions listed, which are caused by specific gene defects and have been targets for gene therapy, cri du chat syndrome's basis in a chromosomal deletion makes it not currently treatable with gene therapy methods. Gene therapy typically targets specific gene mutations rather than large chromosomal abnormalities.

Which One of the Following Diseases or Disorders Has Not