Which of the following is an example of gene therapy?
A) replacing a failing heart with a new heart from a genetically matched donor
B) injecting human factor VIII protein into hemophiliacs with a defective factor VIII gene
C) infecting a cystic fibrosis patient with a virus carrying a working copy of the cystic fibrosis gene
D) providing therapeutic drugs to a patient experiencing high blood pressure

Question

Quizplus · Accepted Answer

Gene therapy involves introducing a working copy of a defective gene into a patient's cells to treat or cure a genetic disorder. Option C describes this process by infecting a cystic fibrosis patient with a virus carrying a working copy of the cystic fibrosis gene. A and D are not examples of gene therapy, as they involve replacing organs or providing drugs to manage symptoms, respectively. Option B describes protein therapy, which involves providing a missing or defective protein to a patient, rather than addressing the underlying genetic cause of their condition.

Which of the Following Is an Example of Gene Therapy